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🧬 Genetic Analysis
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📊 Resource Allocation by Research Phase:
📚 Data Analysis
🧪 Experimental Design
🔬 Clinical Trials
💊 Treatment Development
This is a long-term follow-up safety and efficacy study of participants in ...
Status
Active Not Recruiting
Location
Stanford University Medical Center
Start Date
2020-02-10
Trial ID
NCT04042025
Treatments Being Tested
The purpose of this trial is to evaluate the safety and tolerability of int...
Status
Terminated
Location
UCLA
Start Date
2017-12-14
Trial ID
NCT03381729
Treatments Being Tested
To evaluate the safety and efficacy of intravenous onasemnogene abeparvovec...
Status
Completed
Location
David Geffen School of Medicine at UCLA
Start Date
2018-04-02
Trial ID
NCT03505099
Treatments Being Tested
This is a Phase 3, open-label, single-arm, single-dose, trial of onasemnoge...
Status
Completed
Location
Tokyo Women's Medical University
Start Date
2019-05-31
Trial ID
NCT03837184
Treatments Being Tested
Phase 3 pivotal US trial studying open-label intravenous administration of ...
Status
Completed
Location
David Geffen School of Medicine at UCLA
Start Date
2017-10-24
Trial ID
NCT03306277
Treatments Being Tested
Phase 3, open-label, single-arm, single-dose, trial of onasemnogene abeparv...
Status
Completed
Location
University Hospital Ghent Neuromuscular reference center
Start Date
2018-08-16
Trial ID
NCT03461289
Treatments Being Tested
This double-blind, Phase 2, multiple-dose study will be conducted to evalua...
Status
Recruiting
Location
Phoenix Children's Hospital
Start Date
2025-09-15
Trial ID
NCT07047144
Treatments Being Tested
This is a long term, safety follow up study of patients in the AVXS-101-CL-...
Status
Active Not Recruiting
Location
Nationwide Children's Hospital
Start Date
2017-09-21
Trial ID
NCT03421977
Treatments Being Tested